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Acadia Pharmaceuticals USD 1.61B 41.04M 2026-03
Agios Pharmaceuticals USD 1.18B 112.24M 2026-03
Alnylam Pharmaceuticals USD 5.13B 163.22M 2026-03
BioCryst Pharmaceuticals USD 465.05M 49.11M 2026-03
BioMarin Pharmaceutical USD 8.59B 996.99M 2026-03
Esperion Therapeutics USD 462.53M 3.36M 2026-03
Immunic USD 189.74M 165.69M 2026-03
Insmed USD 2.08B 188.7M 2026-03
Ionis Pharmaceuticals USD 3.45B 74M 2026-03
Karyopharm Therapeutics USD 108.42M 12.18M 2025-12
Kyowa Hakko Kirin JPY 1.07T 40.7B 2026-03
MacroGenics USD 256.85M 13.92M 2025-12
Moderna USD 11.49B 850M 2026-03
Neurocrine Biosciences USD 4.91B 274.7M 2026-03
PTC Therapeutics USD 2.87B 29.66M 2026-03
Puma Biotechnology USD 202.86M 7.95M 2025-09
Regeneron Pharmaceuticals USD 40.87B 310.1M 2026-03
Sarepta Therapeutics USD 3.18B 170.77M 2026-03
Ultragenyx Pharmaceutical USD 1.3B 236M 2026-03
Vertex Pharmaceuticals USD 26.48B 841.4M 2026-03
Xoma USD 263.15M 39.7M 2025-09